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Article info
Publication history
Footnotes
The authors report no conflicts.
Mr. J.T.K. is a medical student at the University of Alabama at Birmingham. Ms. J.B.L. is a paid consultant at Rettsyndrome.org regarding clinical matter related to Rett syndrome and is funded by NIH U54 grant HD061222. H.-S.L. is a statistician for the Rare Disease Clinical Research Network at the University of South Florida Data Management and Coordinating Center. Mr. J.H.P. is a medical student at the University of Alabama at Birmingham. Dr. S.A.S. serves on the Scientific Advisory Board of Rettsyndrome.org and is funded by NIH U54 grant HD061222. Dr. W.E.K. serves on the Scientific Advisory Board of Rettsyndrome.org, receives grant funding from Rettsyndrome.org for the IGF-1 clinical trial, and is funded by NIH U54 grant HD061222. Dr. D.G.G. serves on the Scientific Advisory Board of Rettsyndrome.org, is funded by NIH U54 grant HD061222 and the Blue Bird Circle in Houston for studies related to Rett syndrome, and was an investigator on the Neuren Pharmaceuticals clinical trial for Rett syndrome (NNZ-2566) which concluded in 2014. Dr. J.L.N. serves on the Scientific Advisory Board of Rettsyndrome.org, receives grant funding from Rettsyndrome.org for the research studies related to Rett syndrome, is funded by NIH U54 grant HD061222 of which he is the Administrative Leader, and was an investigator on the Neuren Pharmaceuticals clinical trial for Rett syndrome (NNZ-2566) which concluded in 2014. Dr. A.K.P. serves on the Scientific Advisory Board of Rettsyndrome.org, is the principal investigator of the Rare Diseases Clinical Research Center grant for Rett syndrome, MECP2 Duplication Disorder, and Rett-related Disorders grant, HD061222 (NICHD and NINDS), is funded by NIH U54 grant HD061222, receives administrative support from the Civitan International Research Center, and was an investigator on the Neuren Pharmaceuticals clinical trial for Rett syndrome (NNZ-2566) which concluded in 2014.
